r/Zevra Jul 16 '25

Zevra Therapeutics Announces Open Label Extension Data Showing Sustained Long-Term Efficacy Of MIPLYFFA For The Treatment Of NPC Published In The Journal Of Molecular Genetics And Metabolism

https://investors.zevra.com/news-releases/news-release-details/zevra-therapeutics-announces-open-label-extension-data-showing
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